Splicing mutations in the CFTR gene as therapeutic targets
Karine Deletang1 and Magali Taulan-Cadars – Gene Therapy (2022) 29:399–406
miRNA repertoires of cystic fibrosis ex vivo models highlight miR-181a and miR-101 that regulate WISP1 expression
– Alexandra Pommier, Jessica Varilh, Solenne Bleuse, Karine Delétang, Jennifer Bonini, Anne Bergougnoux, Emmanuelle Brochiero, Michel Koenig, Mireille Claustres, Magali Taulan-Cadars
Transcription factors and miRNAs that regulate fetal to adult CFTR expression change are new targets for cystic fibrosis
DOI: 10.1183/09031936.00113214 – Victoria Viart1,2,3, Anne Bergougnoux1,3, Jennifer Bonini1,2, Jessica Varilh1,3, Raphaël Chiron4, Olivier Tabary5,6, Nicolas Molinari7,8, Mireille Claustres1,2,3 and Magali Taulan-Cadars1,2.